Retrospective outcomes studies for orphan diseases: challenges and opportunities.
Curr Med Res Opin. 2012.
PMID: 22432785
Search Page
Filters
Results by year
Table representation of search results timeline featuring number of search results per year.
| Year | Number of Results |
|---|---|
| 2003 | 1 |
| 2012 | 1 |
| 2015 | 1 |
| 2016 | 1 |
| 2017 | 1 |
| 2024 | 1 |
Search Results
6 results
Results by year
Citations
1
article
found by citation matching
Search results
Page 1
Did you mean
retrospective outcome studies for orphan diseases: challenges and opportunities
(3 results)?
Retrospective outcomes studies for orphan diseases: challenges and opportunities.
Curr Med Res Opin. 2012 Apr;28(4):665-7. doi: 10.1185/03007995.2012.673480. Epub 2012 Mar 20.
Curr Med Res Opin. 2012.
PMID: 22432785
Retrospective outcomes studies for orphan diseases are scarce in the literature because of the significant methodological and data challenges that researchers have to overcome. ...With the introduction of two retrospective orpha …
Retrospective outcomes studies for orphan diseases are scarce in the literature because of the significan …
Primary Immune Deficiency Treatment Consortium (PIDTC) update.
J Allergy Clin Immunol. 2016 Aug;138(2):375-85. doi: 10.1016/j.jaci.2016.01.051. Epub 2016 Apr 22.
J Allergy Clin Immunol. 2016.
PMID: 27262745
Free PMC article.
Review.
An additional 3 European centers have partnered with the PIDTC to study CGD. Natural history protocols of the PIDTC analyze outcomes of treatment for rare PIDs in multicenter longitudinal retrospective, prospective, and cross-sectional studies. ...Fund …
An additional 3 European centers have partnered with the PIDTC to study CGD. Natural history protocols of the PIDTC analyze outcomes …
Paediatric heart transplantation: life-saving but not yet a cure.
Cardiol Young. 2024 Feb;34(2):233-237. doi: 10.1017/S1047951123004146. Epub 2024 Jan 23.
Cardiol Young. 2024.
PMID: 38258454
Addressing these challenges faces the reality that for-profit research favours funding adult recipients, with 10-fold greater numbers, and their more modest longevity goals. Advocacy for funding "incentives" such as the Orphan Drug rules in the United States and uph …
Addressing these challenges faces the reality that for-profit research favours funding adult recipients, with 10-fold greater numbers …
Interventional Bronchoscopic Therapy in Adult Patients with Tracheobronchial Mucoepidermoid Carcinoma.
Chin Med J (Engl). 2017 Oct 20;130(20):2453-2458. doi: 10.4103/0366-6999.216417.
Chin Med J (Engl). 2017.
PMID: 29052567
Free PMC article.
BACKGROUND: Tracheobronchial mucoepidermoid carcinoma (MEC) is a rare airway tumor in adults for which surgery is considered a first-line treatment. ...METHODS: We retrospectively analyzed the clinical manifestations, bronchoscopic interventions, complications, and …
BACKGROUND: Tracheobronchial mucoepidermoid carcinoma (MEC) is a rare airway tumor in adults for which surgery is considered a first- …
Pulmonary disease caused by M. malmoense in HIV negative patients: 5-yr follow-up of patients receiving standardised treatment.
Eur Respir J. 2003 Mar;21(3):478-82.
Eur Respir J. 2003.
PMID: 12662005
Free article.
The literature concerning the management of pulmonary disease caused by Mycobacterium malmoense consists of retrospective reports on small series of patients. A recent multicentre trial conducted by the British Thoracic Society provided an opportunity to prospective …
The literature concerning the management of pulmonary disease caused by Mycobacterium malmoense consists of retrospective reports on …
GHOST Protocol: Greatest Healing Opportunity for Soft Tissue, a Treatment Paradigm for Complex Sarcoma Reconstruction.
Am Surg. 2015 Jun;81(6):557-63.
Am Surg. 2015.
PMID: 26031266
In addition to evaluating clinical outcomes, cases were reviewed to identify factors associated with excellent or poor patient care. Review of these cases formed the basis of the greatest healing opportunity for soft tissue (GHOST) protocol. Our patient popul …
In addition to evaluating clinical outcomes, cases were reviewed to identify factors associated with excellent or poor patient car …
Cite